This baby was the world's first ever healed with a personalized gene editing treatment www.nytimes.com/2025/05/15/h... BEFORE "KJ’s disease is caused by an inability to rid the body of ammonia, a byproduct of protein metabolism. Ammonia builds up in the blood and crosses into the brain. His doctors put him on a diet that severely restricted protein — just enough for him to grow. He also had a medicine that helped remove the ammonia in his blood. But he still was at high risk for brain injury or death. Any illness could make his ammonia levels soar and cause irreversible damage to his brain." AFTER "It is too soon to know if he can stop taking the medication completely, but the dosage is greatly reduced. And he is well enough for the team to start planning to discharge him home from the hospital. He is meeting milestones and his weight is now in the 40th percentile for his age, but it is not yet known if he’ll be spared a liver transplant."
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Karo K avatar
Reading about KJ Muldoon’s groundbreaking treatment fills me with a profound sense of hope. The rapid development of a personalized gene-editing therapy using CRISPR base editing to correct a single DNA mutation in just six months is nothing short of revolutionary. As someone navigating the complexities of chronic ill
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keccers avatar
I always get a little sad because I don’t feel like these types of things will ever become accessible 🥲
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Karo K avatar
ugh yeah… it’s hard not to go a little doomsday about it. $800k for a treatment that isn’t guaranteed? it breaks my heart thinking about how many families will go into debt just to try and save their child. i’ve been feeling that weight too but also feeling more motivated than ever. i can’t wait to start building something of my own that could help shift this. even a little.
ted (not lasso) avatar
A Gene-Editing Breakthrough Saves Infant With Rare Disease https://www.wsj.com/tech/bi...
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clone.fyi avatar
CRISPR MAXIIIIIII
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keccers avatar
MINUTES BEHIND. SHAME ON ME, NEED TO GET GUD 😆
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ted (not lasso) avatar
just quote cast @clone instead!!!!
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keccers avatar
No disrespect but I am failing if I don’t beat them to the scoop
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Oƚƚι🏴‍☠️ avatar
But how
shairaaa avatar
A miracle and blessed baby indeed
Your_Tech_Sis avatar
Miraculous baby
AivyX avatar
cute baby, wish him all the best
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