This baby was the world's first ever healed with a personalized gene editing treatment https://www.nytimes.com/2025/05/15/health/gene-editing-personalized-rare-disorders.html

BEFORE
"KJ’s disease is caused by an inability to rid the body of ammonia, a byproduct of protein metabolism. Ammonia builds up in the blood and crosses into the brain. His doctors put him on a diet that severely restricted protein — just enough for him to grow. He also had a medicine that helped remove the ammonia in his blood. But he still was at high risk for brain injury or death. Any illness could make his ammonia levels soar and cause irreversible damage to his brain."

AFTER
"It is too soon to know if he can stop taking the medication completely, but the dosage is greatly reduced. And he is well enough for the team to start planning to discharge him home from the hospital. He is meeting milestones and his weight is now in the 40th percentile for his age, but it is not yet known if he’ll be spared a liver transplant."

Science

Reading about KJ Muldoon’s groundbreaking treatment fills me with a profound sense of hope. The rapid development of a personalized gene-editing therapy using CRISPR base editing to correct a single DNA mutation in just six months is nothing short of revolutionary.

As someone navigating the complexities of chronic illness, this advancement resonates deeply. It signifies a future where treatments are tailored to individual genetic profiles, offering solutions to conditions previously deemed untreatable. The success of KJ’s therapy not only showcases the potential of precision medicine but also highlights the collaborative effort of scientists, clinicians, and families in pushing the boundaries of what’s possible.

While challenges remain in making such therapies widely accessible, this milestone is a testament to human ingenuity and compassion. It inspires me to believe in a future where personalized medicine becomes the norm, bringing healing and hope to countless others.

Link to article below:

https://warpcast.com/serendipity/0xd6e269ea my thoughts :)

The Farcaster formerly known as Kchamp. Books, beats, bodybuilding, bright ideas and beautiful things.

katherinechampagne.com

Founder of /fcny - 50+ IRL events for Farcaster's builder ecosystem | Systems + community strategy

I always get a little sad because I don’t feel like these types of things will ever become accessible 🥲

ugh yeah… it’s hard not to go a little doomsday about it. $800k for a treatment that isn’t guaranteed? it breaks my heart thinking about how many families will go into debt just to try and save their child.

i’ve been feeling that weight too but also feeling more motivated than ever. i can’t wait to start building something of my own that could help shift this. even a little.